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VMAT2 Inhibitors and Tardive Dyskinesia

Sep 20, 2025

Overview

This lecture explains how VMAT2 inhibitors treat tardive dyskinesia by reducing dopamine activity in the motor striatum to rebalance motor control.

VMAT2 Function and Inhibition

  • VMAT2 transports monoamines (dopamine, serotonin, norepinephrine, histamine) into synaptic vesicles for neurotransmitter storage and release.
  • Tetrabenazine and related drugs selectively and reversibly inhibit VMAT2 in the CNS, leading to reduced dopamine storage and release.
  • VMAT2 inhibition preferentially decreases dopamine levels at clinical doses, causing presynaptic dopamine degradation by monoamine oxidase (MAO).

Pathophysiology of Tardive Dyskinesia (TD)

  • Chronic D2 dopamine receptor blockade leads to supersensitive D2 receptors in the motor striatum via maladaptive neuronal plasticity.
  • This receptor supersensitivity results in excessive inhibition of stop signals and unopposed go signals, causing involuntary hyperkinetic movements (TD).

Therapeutic Mechanism of VMAT2 Inhibitors in TD

  • VMAT2 inhibitors decrease dopamine release, reducing overactivation of supersensitive D2 receptors in the indirect motor pathway ("stop" signal).
  • Dopamine reduction also lessens stimulation of D1 receptors in the direct pathway, weakening "go" signals.
  • The combined effect is increased stop and decreased go signaling, reducing abnormal movements.

Treatment Considerations and Variables

  • Dosing and effectiveness of VMAT2 inhibitors depend on ongoing use, dose, or discontinuation of D2 antagonists.
  • The degree of inhibition needed varies by individual factors: presynaptic dopamine concentration, D2 receptor sensitivity, concurrent drugs, and disease state.
  • VMAT2 inhibition is reversible and responsive to changes in dopamine levels due to external factors (e.g., stress, amphetamines).

Key Terms & Definitions

  • VMAT2 (Vesicular Monoamine Transporter 2) — protein that loads monoamine neurotransmitters into vesicles for release.
  • Tetrabenazine — drug that reversibly inhibits VMAT2, reducing dopamine storage/release in the CNS.
  • D2 Receptor — dopamine receptor involved in the indirect pathway of movement control; upregulated in TD.
  • Indirect Pathway — neural pathway reinforcing motor "stop" signals, disrupted in TD.
  • Direct Pathway — pathway reinforcing motor "go" signals, also influenced by dopamine.

Action Items / Next Steps

  • Review neural pathways of movement control and the role of dopamine in TD.
  • Study the clinical uses and pharmacology of VMAT2 inhibitors for exam preparation.